Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy.

Foley AR, Yun P, Leach ME, Neuhaus SB, Averion GV, Hu Y, Hayes LH, Donkervoort S, Jain MS, Waite M, Parks R, Bharucha-Goebel DX, Mayer OH, Zou Y, Fink M, DeCoster J, Mendoza C, Arévalo C, Hausmann R, Petraki D, Cheung K, Bönnemann CG

Open source

DOI: 10.1212/nxg.0000000000200148
Published: 2024 Jun
Container: Neurology. Genetics
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1212/nxg.0000000000200148,
  title = {Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy.},
  author = {Foley AR and Yun P and Leach ME and Neuhaus SB and Averion GV and Hu Y and Hayes LH and Donkervoort S and Jain MS and Waite M and Parks R and Bharucha-Goebel DX and Mayer OH and Zou Y and Fink M and DeCoster J and Mendoza C and Arévalo C and Hausmann R and Petraki D and Cheung K and Bönnemann CG},
  year = {2024},
  journal = {Neurology. Genetics},
  doi = {10.1212/nxg.0000000000200148},
  url = {https://doi.org/10.1212/nxg.0000000000200148}
}

RIS

TY  - JOUR
TI  - Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy.
AU  - Foley AR
AU  - Yun P
AU  - Leach ME
AU  - Neuhaus SB
AU  - Averion GV
AU  - Hu Y
AU  - Hayes LH
AU  - Donkervoort S
AU  - Jain MS
AU  - Waite M
AU  - Parks R
AU  - Bharucha-Goebel DX
AU  - Mayer OH
AU  - Zou Y
AU  - Fink M
AU  - DeCoster J
AU  - Mendoza C
AU  - Arévalo C
AU  - Hausmann R
AU  - Petraki D
AU  - Cheung K
AU  - Bönnemann CG
PY  - 2024
JO  - Neurology. Genetics
DO  - 10.1212/nxg.0000000000200148
UR  - https://doi.org/10.1212/nxg.0000000000200148
ER  -

APA

AR, F., P, Y., ME, L., SB, N., GV, A., Y, H., LH, H., S, D., MS, J., M, W., R, P., DX, B., OH, M., Y, Z., M, F., J, D., C, M., C, A., R, H., D, P., K, C., & CG, B. (2024). Phase 1 Open-Label Study of Omigapil in Patients With LAMA2- or COL6-Related Dystrophy.. Neurology. Genetics. https://doi.org/10.1212/nxg.0000000000200148

Source records

pubmed · retrieved 2026-09-27T01:18:46.874Z