Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy

Hugh J. McMillan, Giovanni Baranello, Michelle A. Farrar, Craig M. Zaidman, Teresa Moreno, Liesbeth De Waele, Yuh-Jyh Jong, Vincent Laugel, Susana Quijano-Roy, Eugenio Mercuri, Yin-Hsiu Chien, Volker Straub, Basil T. Darras, Julia Seibert, Roberto Bernardo Escudero, Iulian Alecu, Frank Freischläger, Francesco Muntoni, Unknown

Open source

DOI: 10.1212/wnl.0000000000210268
Published: 2025-01-28
Container: Neurology
Publisher: Ovid Technologies (Wolters Kluwer Health)
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.1212/wnl.0000000000210268,
  title = {Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy},
  author = {Hugh J. McMillan and Giovanni Baranello and Michelle A. Farrar and Craig M. Zaidman and Teresa Moreno and Liesbeth De Waele and Yuh-Jyh Jong and Vincent Laugel and Susana Quijano-Roy and Eugenio Mercuri and Yin-Hsiu Chien and Volker Straub and Basil T. Darras and Julia Seibert and Roberto Bernardo Escudero and Iulian Alecu and Frank Freischläger and Francesco Muntoni and Unknown},
  year = {2025},
  journal = {Neurology},
  doi = {10.1212/wnl.0000000000210268},
  url = {https://doi.org/10.1212/wnl.0000000000210268}
}

RIS

TY  - JOUR
TI  - Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy
AU  - Hugh J. McMillan
AU  - Giovanni Baranello
AU  - Michelle A. Farrar
AU  - Craig M. Zaidman
AU  - Teresa Moreno
AU  - Liesbeth De Waele
AU  - Yuh-Jyh Jong
AU  - Vincent Laugel
AU  - Susana Quijano-Roy
AU  - Eugenio Mercuri
AU  - Yin-Hsiu Chien
AU  - Volker Straub
AU  - Basil T. Darras
AU  - Julia Seibert
AU  - Roberto Bernardo Escudero
AU  - Iulian Alecu
AU  - Frank Freischläger
AU  - Francesco Muntoni
AU  - Unknown
PY  - 2025
JO  - Neurology
DO  - 10.1212/wnl.0000000000210268
UR  - https://doi.org/10.1212/wnl.0000000000210268
ER  -

APA

McMillan, H. J., Baranello, G., Farrar, M. A., Zaidman, C. M., Moreno, T., Waele, L. D., Jong, Y., Laugel, V., Quijano-Roy, S., Mercuri, E., Chien, Y., Straub, V., Darras, B. T., Seibert, J., Escudero, R. B., Alecu, I., Freischläger, F., Muntoni, F., & Unknown (2025). Safety and Efficacy of IV Onasemnogene Abeparvovec for Pediatric Patients With Spinal Muscular Atrophy. Neurology. https://doi.org/10.1212/wnl.0000000000210268

Source records

crossref · retrieved 2026-09-26T11:34:20.763Z