Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.
- DOI
- 10.1212/wnl.0000000000218066
- Published
- 2026 Jun 9
- Container
- Neurology
- Publisher
- Not recorded
- Open access
- yes
Credibility signals
limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.
Show all credibility signals
- cautionDOI registered: No matching Crossref record was present in this response.
- cautionDOI resolves: No matching Crossref record was present in this response.
- not scoredDirectory of Open Access Journals: No matching DOAJ record was present in this response. No allow-list match; this is not evidence of low credibility.
- not scoredMEDLINE indexed: Not checked or no result supplied; no credibility inference made.
- not scoredOpenAlex core source: Not checked or no result supplied; no credibility inference made.
- not scoredKnown publisher allow-list: Not checked or no result supplied; no credibility inference made.
- not scoredROR affiliation: Not checked or no result supplied; no credibility inference made.
- not scoredRetraction Watch retraction: No retraction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch expression of concern: No expression of concern notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch correction: No correction notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- not scoredRetraction Watch reinstatement: No reinstatement notice matched this DOI in the deployed snapshot. No matching event found; coverage may be incomplete.
- supportingOpen access status: Normalized open-access status: open.
- not scoredPublication license: Not checked or no result supplied; no credibility inference made.
- not scoredPublication version: A publication version was supplied but is not scored.
- cautionMetadata completeness: 5 of 6 scored descriptive metadata groups are present; missing fields increase uncertainty.
Cite this work
BibTeX
@article{allodium:10.1212/wnl.0000000000218066,
title = {Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.},
author = {Mah JK and Gonorazky HD and Nigro E and Lochmüller H and Alemán A and Yaworski A and Oskoui M and Sbrocchi AM and Selby KA and de Vera A and Mathur R and Gresko E and Linden A and Dutreix C and Hoffman EP},
year = {2026},
journal = {Neurology},
doi = {10.1212/wnl.0000000000218066},
url = {https://doi.org/10.1212/wnl.0000000000218066}
}RIS
TY - JOUR TI - Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys. AU - Mah JK AU - Gonorazky HD AU - Nigro E AU - Lochmüller H AU - Alemán A AU - Yaworski A AU - Oskoui M AU - Sbrocchi AM AU - Selby KA AU - de Vera A AU - Mathur R AU - Gresko E AU - Linden A AU - Dutreix C AU - Hoffman EP PY - 2026 JO - Neurology DO - 10.1212/wnl.0000000000218066 UR - https://doi.org/10.1212/wnl.0000000000218066 ER -
APA
JK, M., HD, G., E, N., H, L., A, A., A, Y., M, O., AM, S., KA, S., A, D. V., R, M., E, G., A, L., C, D., & EP, H. (2026). Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.. Neurology. https://doi.org/10.1212/wnl.0000000000218066
Source records
- pubmed · retrieved 2026-09-27T01:19:41.727Z