Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency.

Pratt SL, Zarate-Mendez M, Koludarova L, Jansson S, Airavaara M, Hlushchuk I, Coleman D, Heffner C, Horvath R, Battersby BJ, Burgess RW

Open source

DOI: 10.1242/dmm.052120
Published: 2025 May 1
Container: Disease models & mechanisms
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1242/dmm.052120,
  title = {Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency.},
  author = {Pratt SL and Zarate-Mendez M and Koludarova L and Jansson S and Airavaara M and Hlushchuk I and Coleman D and Heffner C and Horvath R and Battersby BJ and Burgess RW},
  year = {2025},
  journal = {Disease models \& mechanisms},
  doi = {10.1242/dmm.052120},
  url = {https://doi.org/10.1242/dmm.052120}
}

RIS

TY  - JOUR
TI  - Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency.
AU  - Pratt SL
AU  - Zarate-Mendez M
AU  - Koludarova L
AU  - Jansson S
AU  - Airavaara M
AU  - Hlushchuk I
AU  - Coleman D
AU  - Heffner C
AU  - Horvath R
AU  - Battersby BJ
AU  - Burgess RW
PY  - 2025
JO  - Disease models & mechanisms
DO  - 10.1242/dmm.052120
UR  - https://doi.org/10.1242/dmm.052120
ER  -

APA

SL, P., M, Z., L, K., S, J., M, A., I, H., D, C., C, H., R, H., BJ, B., & RW, B. (2025). Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency.. Disease models & mechanisms. https://doi.org/10.1242/dmm.052120

Source records

pubmed · retrieved 2026-09-25T11:19:26.180Z