Current Status of Cellular and Gene-Based Therapies for Congenital Metabolic Disorders: A Review.

Masiarz A, Kosteczko P, Mazur M, Pelczar P, Kimber-Trojnar Ż, Leszczyńska-Gorzelak B.

DOI: 10.12659/msm.954145
Published: 2026-09-15
Container: Med Sci Monit
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.12659/msm.954145,
  title = {Current Status of Cellular and Gene-Based Therapies for Congenital Metabolic Disorders: A Review.},
  author = {Masiarz A and  Kosteczko P and  Mazur M and  Pelczar P and  Kimber-Trojnar Ż and  Leszczyńska-Gorzelak B.},
  year = {2026},
  journal = {Med Sci Monit},
  doi = {10.12659/msm.954145},
  url = {https://doi.org/10.12659/msm.954145}
}

RIS

TY  - JOUR
TI  - Current Status of Cellular and Gene-Based Therapies for Congenital Metabolic Disorders: A Review.
AU  - Masiarz A
AU  -  Kosteczko P
AU  -  Mazur M
AU  -  Pelczar P
AU  -  Kimber-Trojnar Ż
AU  -  Leszczyńska-Gorzelak B.
PY  - 2026
JO  - Med Sci Monit
DO  - 10.12659/msm.954145
UR  - https://doi.org/10.12659/msm.954145
ER  -

APA

A, M., P, K., M, M., P, P., Ż, K., & B., L. (2026). Current Status of Cellular and Gene-Based Therapies for Congenital Metabolic Disorders: A Review.. Med Sci Monit. https://doi.org/10.12659/msm.954145

Source records

europe-pmc · retrieved 2026-09-25T13:36:43.808Z