Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.

McDonald CM, Signorovitch J, Mercuri E, Niks EH, Wong B, Fillbrunn M, Sajeev G, Yim E, Dieye I, Miller D, Ward SJ, Goemans N, Investigators from the PRO-DMD-01 Study, Collaborative Trajectory Analysis Project (cTAP)

Open source

DOI: 10.1371/journal.pone.0304099
Published: 2024
Container: PloS one
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.1371/journal.pone.0304099,
  title = {Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.},
  author = {McDonald CM and Signorovitch J and Mercuri E and Niks EH and Wong B and Fillbrunn M and Sajeev G and Yim E and Dieye I and Miller D and Ward SJ and Goemans N and Investigators from the PRO-DMD-01 Study, Collaborative Trajectory Analysis Project (cTAP)},
  year = {2024},
  journal = {PloS one},
  doi = {10.1371/journal.pone.0304099},
  url = {https://doi.org/10.1371/journal.pone.0304099}
}

RIS

TY  - JOUR
TI  - Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.
AU  - McDonald CM
AU  - Signorovitch J
AU  - Mercuri E
AU  - Niks EH
AU  - Wong B
AU  - Fillbrunn M
AU  - Sajeev G
AU  - Yim E
AU  - Dieye I
AU  - Miller D
AU  - Ward SJ
AU  - Goemans N
AU  - Investigators from the PRO-DMD-01 Study, Collaborative Trajectory Analysis Project (cTAP)
PY  - 2024
JO  - PloS one
DO  - 10.1371/journal.pone.0304099
UR  - https://doi.org/10.1371/journal.pone.0304099
ER  -

APA

CM, M., J, S., E, M., EH, N., B, W., M, F., G, S., E, Y., I, D., D, M., SJ, W., N, G., & (cTAP), I. F. T. P. S. C. T. A. P. (2024). Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.. PloS one. https://doi.org/10.1371/journal.pone.0304099

Source records

pubmed · retrieved 2026-09-27T12:18:01.326Z
europe-pmc · retrieved 2026-09-27T12:18:01.341Z