Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.

McDonald CM, Muntoni F, Penematsa V, Jiang J, Kristensen A, Bibbiani F, Goodwin E, Gordish-Dressman H, Morgenroth L, Werner C, Li J, Able R, Trifillis P, Tulinius M, Study 019 investigators

Open source

DOI: 10.2217/cer-2021-0196
Published: 2022 Feb
Container: Journal of comparative effectiveness research
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.2217/cer-2021-0196,
  title = {Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.},
  author = {McDonald CM and Muntoni F and Penematsa V and Jiang J and Kristensen A and Bibbiani F and Goodwin E and Gordish-Dressman H and Morgenroth L and Werner C and Li J and Able R and Trifillis P and Tulinius M and Study 019 investigators},
  year = {2022},
  journal = {Journal of comparative effectiveness research},
  doi = {10.2217/cer-2021-0196},
  url = {https://doi.org/10.2217/cer-2021-0196}
}

RIS

TY  - JOUR
TI  - Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.
AU  - McDonald CM
AU  - Muntoni F
AU  - Penematsa V
AU  - Jiang J
AU  - Kristensen A
AU  - Bibbiani F
AU  - Goodwin E
AU  - Gordish-Dressman H
AU  - Morgenroth L
AU  - Werner C
AU  - Li J
AU  - Able R
AU  - Trifillis P
AU  - Tulinius M
AU  - Study 019 investigators
PY  - 2022
JO  - Journal of comparative effectiveness research
DO  - 10.2217/cer-2021-0196
UR  - https://doi.org/10.2217/cer-2021-0196
ER  -

APA

CM, M., F, M., V, P., J, J., A, K., F, B., E, G., H, G., L, M., C, W., J, L., R, A., P, T., M, T., & investigators, S. 0. (2022). Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.. Journal of comparative effectiveness research. https://doi.org/10.2217/cer-2021-0196

Source records

pubmed · retrieved 2026-09-25T21:59:10.117Z
europe-pmc · retrieved 2026-09-25T21:59:10.133Z
hal · retrieved 2026-09-25T21:59:10.168Z