Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database.

Koeks Z, Bladen CL, Salgado D, van Zwet E, Pogoryelova O, McMacken G, Monges S, Foncuberta ME, Kekou K, Kosma K, Dawkins H, Lamont L, Bellgard MI, Roy AJ, Chamova T, Guergueltcheva V, Chan S, Korngut L, Campbell C, Dai Y, Wang J, Barišić N, Brabec P, Lähdetie J, Walter MC, Schreiber-Katz O, Karcagi V, Garami M, Herczegfalvi A, Viswanathan V, Bayat F, Buccella F, Ferlini A, Kimura E, van den Bergen JC, Rodrigues M, Roxburgh R, Lusakowska A, Kostera-Pruszczyk A, Santos R, Neagu E, Artemieva S, Rasic VM, Vojinovic D, Posada M, Bloetzer C, Klein A, Díaz-Manera J, Gallardo E, Karaduman AA, Oznur T, Topaloğlu H, El Sherif R, Stringer A, Shatillo AV, Martin AS, Peay HL, Kirschner J, Flanigan KM, Straub V, Bushby K, Béroud C, Verschuuren JJ, Lochmüller H

Open source

DOI: 10.3233/jnd-170280
Published: 2017
Container: Journal of neuromuscular diseases
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.3233/jnd-170280,
  title = {Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database.},
  author = {Koeks Z and Bladen CL and Salgado D and van Zwet E and Pogoryelova O and McMacken G and Monges S and Foncuberta ME and Kekou K and Kosma K and Dawkins H and Lamont L and Bellgard MI and Roy AJ and Chamova T and Guergueltcheva V and Chan S and Korngut L and Campbell C and Dai Y and Wang J and Barišić N and Brabec P and Lähdetie J and Walter MC and Schreiber-Katz O and Karcagi V and Garami M and Herczegfalvi A and Viswanathan V and Bayat F and Buccella F and Ferlini A and Kimura E and van den Bergen JC and Rodrigues M and Roxburgh R and Lusakowska A and Kostera-Pruszczyk A and Santos R and Neagu E and Artemieva S and Rasic VM and Vojinovic D and Posada M and Bloetzer C and Klein A and Díaz-Manera J and Gallardo E and Karaduman AA and Oznur T and Topaloğlu H and El Sherif R and Stringer A and Shatillo AV and Martin AS and Peay HL and Kirschner J and Flanigan KM and Straub V and Bushby K and Béroud C and Verschuuren JJ and Lochmüller H},
  year = {2017},
  journal = {Journal of neuromuscular diseases},
  doi = {10.3233/jnd-170280},
  url = {https://doi.org/10.3233/jnd-170280}
}

RIS

TY  - JOUR
TI  - Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database.
AU  - Koeks Z
AU  - Bladen CL
AU  - Salgado D
AU  - van Zwet E
AU  - Pogoryelova O
AU  - McMacken G
AU  - Monges S
AU  - Foncuberta ME
AU  - Kekou K
AU  - Kosma K
AU  - Dawkins H
AU  - Lamont L
AU  - Bellgard MI
AU  - Roy AJ
AU  - Chamova T
AU  - Guergueltcheva V
AU  - Chan S
AU  - Korngut L
AU  - Campbell C
AU  - Dai Y
AU  - Wang J
AU  - Barišić N
AU  - Brabec P
AU  - Lähdetie J
AU  - Walter MC
AU  - Schreiber-Katz O
AU  - Karcagi V
AU  - Garami M
AU  - Herczegfalvi A
AU  - Viswanathan V
AU  - Bayat F
AU  - Buccella F
AU  - Ferlini A
AU  - Kimura E
AU  - van den Bergen JC
AU  - Rodrigues M
AU  - Roxburgh R
AU  - Lusakowska A
AU  - Kostera-Pruszczyk A
AU  - Santos R
AU  - Neagu E
AU  - Artemieva S
AU  - Rasic VM
AU  - Vojinovic D
AU  - Posada M
AU  - Bloetzer C
AU  - Klein A
AU  - Díaz-Manera J
AU  - Gallardo E
AU  - Karaduman AA
AU  - Oznur T
AU  - Topaloğlu H
AU  - El Sherif R
AU  - Stringer A
AU  - Shatillo AV
AU  - Martin AS
AU  - Peay HL
AU  - Kirschner J
AU  - Flanigan KM
AU  - Straub V
AU  - Bushby K
AU  - Béroud C
AU  - Verschuuren JJ
AU  - Lochmüller H
PY  - 2017
JO  - Journal of neuromuscular diseases
DO  - 10.3233/jnd-170280
UR  - https://doi.org/10.3233/jnd-170280
ER  -

APA

Z, K., CL, B., D, S., E, V. Z., O, P., G, M., S, M., ME, F., K, K., K, K., H, D., L, L., MI, B., AJ, R., T, C., V, G., S, C., L, K., C, C., Y, D., J, W., N, B., P, B., J, L., MC, W., O, S., V, K., M, G., A, H., V, V., F, B., F, B., A, F., E, K., JC, V. D. B., M, R., R, R., A, L., A, K., R, S., E, N., S, A., VM, R., D, V., M, P., C, B., A, K., J, D., E, G., AA, K., T, O., H, T., R, E. S., A, S., AV, S., AS, M., HL, P., J, K., KM, F., V, S., K, B., C, B., JJ, V., & H, L. (2017). Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database.. Journal of neuromuscular diseases. https://doi.org/10.3233/jnd-170280

Source records

pubmed · retrieved 2026-11-10T18:56:52.835Z
europe-pmc · retrieved 2026-11-10T18:56:52.832Z
hal · retrieved 2026-11-10T18:56:52.881Z
hal · retrieved 2026-11-10T18:56:52.881Z