INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy

James J. Dowling, Unknown, Wolfgang Müller-Felber, Barbara K. Smith, Carsten G. Bönnemann, Nancy L. Kuntz, Francesco Muntoni, Laurent Servais, Lindsay N. Alfano, Alan H. Beggs, Deborah A. Bilder, Astrid Blaschek, Tina Duong, Robert J. Graham, Minal Jain, Michael W. Lawlor, Jun Lee, Julie Coats, Charlotte Lilien, Linda P. Lowes, Victoria MacBean, Sarah Neuhaus, Mojtaba Noursalehi, Teresa Pitts, Caroline Finlay, Sarah Christensen, Gerrard Rafferty, Andreea M. Seferian, Etsuko Tsuchiya, Emma S. James, Weston Miller, Bryan Sepulveda, Maria Candida Vila, Suyash Prasad, Salvador Rico, Perry B. Shieh

Open source

DOI: 10.3233/jnd-210781
Published: 2022-07-01
Container: Journal of Neuromuscular Diseases
Publisher: SAGE Publications
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.3233/jnd-210781,
  title = {INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy},
  author = {James J. Dowling and Unknown and Wolfgang Müller-Felber and Barbara K. Smith and Carsten G. Bönnemann and Nancy L. Kuntz and Francesco Muntoni and Laurent Servais and Lindsay N. Alfano and Alan H. Beggs and Deborah A. Bilder and Astrid Blaschek and Tina Duong and Robert J. Graham and Minal Jain and Michael W. Lawlor and Jun Lee and Julie Coats and Charlotte Lilien and Linda P. Lowes and Victoria MacBean and Sarah Neuhaus and Mojtaba Noursalehi and Teresa Pitts and Caroline Finlay and Sarah Christensen and Gerrard Rafferty and Andreea M. Seferian and Etsuko Tsuchiya and Emma S. James and Weston Miller and Bryan Sepulveda and Maria Candida Vila and Suyash Prasad and Salvador Rico and Perry B. Shieh},
  year = {2022},
  journal = {Journal of Neuromuscular Diseases},
  doi = {10.3233/jnd-210781},
  url = {https://doi.org/10.3233/jnd-210781}
}

RIS

TY  - JOUR
TI  - INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy
AU  - James J. Dowling
AU  - Unknown
AU  - Wolfgang Müller-Felber
AU  - Barbara K. Smith
AU  - Carsten G. Bönnemann
AU  - Nancy L. Kuntz
AU  - Francesco Muntoni
AU  - Laurent Servais
AU  - Lindsay N. Alfano
AU  - Alan H. Beggs
AU  - Deborah A. Bilder
AU  - Astrid Blaschek
AU  - Tina Duong
AU  - Robert J. Graham
AU  - Minal Jain
AU  - Michael W. Lawlor
AU  - Jun Lee
AU  - Julie Coats
AU  - Charlotte Lilien
AU  - Linda P. Lowes
AU  - Victoria MacBean
AU  - Sarah Neuhaus
AU  - Mojtaba Noursalehi
AU  - Teresa Pitts
AU  - Caroline Finlay
AU  - Sarah Christensen
AU  - Gerrard Rafferty
AU  - Andreea M. Seferian
AU  - Etsuko Tsuchiya
AU  - Emma S. James
AU  - Weston Miller
AU  - Bryan Sepulveda
AU  - Maria Candida Vila
AU  - Suyash Prasad
AU  - Salvador Rico
AU  - Perry B. Shieh
PY  - 2022
JO  - Journal of Neuromuscular Diseases
DO  - 10.3233/jnd-210781
UR  - https://doi.org/10.3233/jnd-210781
ER  -

APA

Dowling, J. J., Unknown, Müller-Felber, W., Smith, B. K., Bönnemann, C. G., Kuntz, N. L., Muntoni, F., Servais, L., Alfano, L. N., Beggs, A. H., Bilder, D. A., Blaschek, A., Duong, T., Graham, R. J., Jain, M., Lawlor, M. W., Lee, J., Coats, J., Lilien, C., Lowes, L. P., MacBean, V., Neuhaus, S., Noursalehi, M., Pitts, T., Finlay, C., Christensen, S., Rafferty, G., Seferian, A. M., Tsuchiya, E., James, E. S., Miller, W., Sepulveda, B., Vila, M. C., Prasad, S., Rico, S., & Shieh, P. B. (2022). INCEPTUS Natural History, Run-in Study for Gene Replacement Clinical Trial in X-Linked Myotubular Myopathy. Journal of Neuromuscular Diseases. https://doi.org/10.3233/jnd-210781

Source records

crossref · retrieved 2026-09-27T00:12:41.686Z