Gene therapy for choroideremia using an adeno-associated viral vector encoding Rab escort protein 1: the REGENERATE open-label trial

Jasmina Cehajic-Kapetanovic, Marco P Bellini, Laura J Taylor, Imran H Yusuf, Taha Soomro, Lyndon da Cruz, Robert E MacLaren

Open source

DOI: 10.3310/wara5730
Published: 2024-05
Container: Efficacy and Mechanism Evaluation
Publisher: National Institute for Health and Care Research
Open access: unknown

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Cite this work

BibTeX

@article{allodium:10.3310/wara5730,
  title = {Gene therapy for choroideremia using an adeno-associated viral vector encoding Rab escort protein 1: the REGENERATE open-label trial},
  author = {Jasmina Cehajic-Kapetanovic and Marco P Bellini and Laura J Taylor and Imran H Yusuf and Taha Soomro and Lyndon da Cruz and Robert E MacLaren},
  year = {2024},
  journal = {Efficacy and Mechanism Evaluation},
  doi = {10.3310/wara5730},
  url = {https://doi.org/10.3310/wara5730}
}

RIS

TY  - JOUR
TI  - Gene therapy for choroideremia using an adeno-associated viral vector encoding Rab escort protein 1: the REGENERATE open-label trial
AU  - Jasmina Cehajic-Kapetanovic
AU  - Marco P Bellini
AU  - Laura J Taylor
AU  - Imran H Yusuf
AU  - Taha Soomro
AU  - Lyndon da Cruz
AU  - Robert E MacLaren
PY  - 2024
JO  - Efficacy and Mechanism Evaluation
DO  - 10.3310/wara5730
UR  - https://doi.org/10.3310/wara5730
ER  -

APA

Cehajic-Kapetanovic, J., Bellini, M. P., Taylor, L. J., Yusuf, I. H., Soomro, T., Cruz, L. D., & MacLaren, R. E. (2024). Gene therapy for choroideremia using an adeno-associated viral vector encoding Rab escort protein 1: the REGENERATE open-label trial. Efficacy and Mechanism Evaluation. https://doi.org/10.3310/wara5730

Source records

crossref · retrieved 2026-09-25T03:27:17.565Z