AAV-Mediated CAG-Targeting Selectively Reduces Polyglutamine-Expanded Protein and Attenuates Disease Phenotypes in a Spinocerebellar Ataxia Mouse Model

Anna Niewiadomska-Cimicka, Lorraine Fievet, Magdalena Surdyka, Ewelina Jesion, Céline Keime, Elisabeth Singer, Aurelie Eisenmann, Zaneta Kalinowska-Poska, Hoa Huu Phuc Nguyen, Agnieszka Fiszer, Maciej Figiel, Yvon Trottier

Open source

DOI
10.3390/ijms25084354
Published
2024-04-15
Container
International Journal of Molecular Sciences
Publisher
Not recorded
Open access
yes

Credibility signals

limited evidence Score 45/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.3390/ijms25084354,
  title = {AAV-Mediated CAG-Targeting Selectively Reduces Polyglutamine-Expanded Protein and Attenuates Disease Phenotypes in a Spinocerebellar Ataxia Mouse Model},
  author = {Anna Niewiadomska-Cimicka and Lorraine Fievet and Magdalena Surdyka and Ewelina Jesion and Céline Keime and Elisabeth Singer and Aurelie Eisenmann and Zaneta Kalinowska-Poska and Hoa Huu Phuc Nguyen and Agnieszka Fiszer and Maciej Figiel and Yvon Trottier},
  year = {2024},
  journal = {International Journal of Molecular Sciences},
  doi = {10.3390/ijms25084354},
  url = {https://doi.org/10.3390/ijms25084354}
}

RIS

TY  - JOUR
TI  - AAV-Mediated CAG-Targeting Selectively Reduces Polyglutamine-Expanded Protein and Attenuates Disease Phenotypes in a Spinocerebellar Ataxia Mouse Model
AU  - Anna Niewiadomska-Cimicka
AU  - Lorraine Fievet
AU  - Magdalena Surdyka
AU  - Ewelina Jesion
AU  - Céline Keime
AU  - Elisabeth Singer
AU  - Aurelie Eisenmann
AU  - Zaneta Kalinowska-Poska
AU  - Hoa Huu Phuc Nguyen
AU  - Agnieszka Fiszer
AU  - Maciej Figiel
AU  - Yvon Trottier
PY  - 2024
JO  - International Journal of Molecular Sciences
DO  - 10.3390/ijms25084354
UR  - https://doi.org/10.3390/ijms25084354
ER  - 

APA

Niewiadomska-Cimicka, A., Fievet, L., Surdyka, M., Jesion, E., Keime, C., Singer, E., Eisenmann, A., Kalinowska-Poska, Z., Nguyen, H. H. P., Fiszer, A., Figiel, M., & Trottier, Y. (2024). AAV-Mediated CAG-Targeting Selectively Reduces Polyglutamine-Expanded Protein and Attenuates Disease Phenotypes in a Spinocerebellar Ataxia Mouse Model. International Journal of Molecular Sciences. https://doi.org/10.3390/ijms25084354

Source records