Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects.

Ayupova AI, Solovyeva VV, Issa SS, Fayoud HJ, Rizvanov AA

DOI: 10.3390/ijms262010107
Published: 2025 Oct 17
Container: International journal of molecular sciences
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.3390/ijms262010107,
  title = {Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects.},
  author = {Ayupova AI and Solovyeva VV and Issa SS and Fayoud HJ and Rizvanov AA},
  year = {2025},
  journal = {International journal of molecular sciences},
  doi = {10.3390/ijms262010107},
  url = {https://doi.org/10.3390/ijms262010107}
}

RIS

TY  - JOUR
TI  - Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects.
AU  - Ayupova AI
AU  - Solovyeva VV
AU  - Issa SS
AU  - Fayoud HJ
AU  - Rizvanov AA
PY  - 2025
JO  - International journal of molecular sciences
DO  - 10.3390/ijms262010107
UR  - https://doi.org/10.3390/ijms262010107
ER  -

APA

AI, A., VV, S., SS, I., HJ, F., & AA, R. (2025). Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects.. International journal of molecular sciences. https://doi.org/10.3390/ijms262010107

Source records

pubmed · retrieved 2026-09-27T07:26:06.548Z