A New Gain-of-Function NLRP1 Variant Is Associated with Inflammasome Activation and Disease Severity in SLC25A38 Congenital Sideroblastic Anemia Case Report

María Sánchez-Villalobos, Eulalia Campos Baños, Elena Martínez-Balsalobre, Miriam Pinilla-Marquínez, Verónica Navarro-Ramírez, Thomas Macartney, Laura Hurtado-Navarro, David Hernández-García, Miguel Blanquer, Pablo Pelegrín, Eduardo Salido-Fierrez, Ana Belén Pérez-Oliva

Open source

DOI
10.3390/jpm16090471
Published
2026-09-15
Container
Journal of Personalized Medicine
Publisher
MDPI AG
Open access
unknown

Credibility signals

uncertain Score 64/100 under policy 1.0.0. This is a metadata assessment, not a judgment of the paper's conclusions.

Show all credibility signals

Cite this work

BibTeX

@article{allodium:10.3390/jpm16090471,
  title = {A New Gain-of-Function NLRP1 Variant Is Associated with Inflammasome Activation and Disease Severity in SLC25A38 Congenital Sideroblastic Anemia Case Report},
  author = {María Sánchez-Villalobos and Eulalia Campos Baños and Elena Martínez-Balsalobre and Miriam Pinilla-Marquínez and Verónica Navarro-Ramírez and Thomas Macartney and Laura Hurtado-Navarro and David Hernández-García and Miguel Blanquer and Pablo Pelegrín and Eduardo Salido-Fierrez and Ana Belén Pérez-Oliva},
  year = {2026},
  journal = {Journal of Personalized Medicine},
  doi = {10.3390/jpm16090471},
  url = {https://doi.org/10.3390/jpm16090471}
}

RIS

TY  - JOUR
TI  - A New Gain-of-Function NLRP1 Variant Is Associated with Inflammasome Activation and Disease Severity in SLC25A38 Congenital Sideroblastic Anemia Case Report
AU  - María Sánchez-Villalobos
AU  - Eulalia Campos Baños
AU  - Elena Martínez-Balsalobre
AU  - Miriam Pinilla-Marquínez
AU  - Verónica Navarro-Ramírez
AU  - Thomas Macartney
AU  - Laura Hurtado-Navarro
AU  - David Hernández-García
AU  - Miguel Blanquer
AU  - Pablo Pelegrín
AU  - Eduardo Salido-Fierrez
AU  - Ana Belén Pérez-Oliva
PY  - 2026
JO  - Journal of Personalized Medicine
DO  - 10.3390/jpm16090471
UR  - https://doi.org/10.3390/jpm16090471
ER  - 

APA

Sánchez-Villalobos, M., Baños, E. C., Martínez-Balsalobre, E., Pinilla-Marquínez, M., Navarro-Ramírez, V., Macartney, T., Hurtado-Navarro, L., Hernández-García, D., Blanquer, M., Pelegrín, P., Salido-Fierrez, E., & Pérez-Oliva, A. B. (2026). A New Gain-of-Function NLRP1 Variant Is Associated with Inflammasome Activation and Disease Severity in SLC25A38 Congenital Sideroblastic Anemia Case Report. Journal of Personalized Medicine. https://doi.org/10.3390/jpm16090471

Source records