Efficacy and Safety of 5-Aminolevulinic Acid Hydrochloride Combined with Sodium Ferrous Citrate in Pediatric Patients with Leigh Syndrome and Central Nervous System Disorders: An Initial Exploratory Trial with a Double-Blind Placebo-Controlled Period, Followed by an Open-Label Period and a Subsequent Long-Term Administration Study.

Abe Y, Hamasaki T, Natsume J, Mogami Y, Murayama K, Shiraishi H, Abe Y, Kumada S, Tanaka R, Ihara K, Sakakibara T, Okazaki Y, Nakagawa H, Takahashi K, Yamauchi M, Nakajima M, Ohtake A

Open source

DOI: 10.3390/life15081168
Published: 2025 Jul 23
Container: Life (Basel, Switzerland)
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.3390/life15081168,
  title = {Efficacy and Safety of 5-Aminolevulinic Acid Hydrochloride Combined with Sodium Ferrous Citrate in Pediatric Patients with Leigh Syndrome and Central Nervous System Disorders: An Initial Exploratory Trial with a Double-Blind Placebo-Controlled Period, Followed by an Open-Label Period and a Subsequent Long-Term Administration Study.},
  author = {Abe Y and Hamasaki T and Natsume J and Mogami Y and Murayama K and Shiraishi H and Abe Y and Kumada S and Tanaka R and Ihara K and Sakakibara T and Okazaki Y and Nakagawa H and Takahashi K and Yamauchi M and Nakajima M and Ohtake A},
  year = {2025},
  journal = {Life (Basel, Switzerland)},
  doi = {10.3390/life15081168},
  url = {https://doi.org/10.3390/life15081168}
}

RIS

TY  - JOUR
TI  - Efficacy and Safety of 5-Aminolevulinic Acid Hydrochloride Combined with Sodium Ferrous Citrate in Pediatric Patients with Leigh Syndrome and Central Nervous System Disorders: An Initial Exploratory Trial with a Double-Blind Placebo-Controlled Period, Followed by an Open-Label Period and a Subsequent Long-Term Administration Study.
AU  - Abe Y
AU  - Hamasaki T
AU  - Natsume J
AU  - Mogami Y
AU  - Murayama K
AU  - Shiraishi H
AU  - Abe Y
AU  - Kumada S
AU  - Tanaka R
AU  - Ihara K
AU  - Sakakibara T
AU  - Okazaki Y
AU  - Nakagawa H
AU  - Takahashi K
AU  - Yamauchi M
AU  - Nakajima M
AU  - Ohtake A
PY  - 2025
JO  - Life (Basel, Switzerland)
DO  - 10.3390/life15081168
UR  - https://doi.org/10.3390/life15081168
ER  -

APA

Y, A., T, H., J, N., Y, M., K, M., H, S., Y, A., S, K., R, T., K, I., T, S., Y, O., H, N., K, T., M, Y., M, N., & A, O. (2025). Efficacy and Safety of 5-Aminolevulinic Acid Hydrochloride Combined with Sodium Ferrous Citrate in Pediatric Patients with Leigh Syndrome and Central Nervous System Disorders: An Initial Exploratory Trial with a Double-Blind Placebo-Controlled Period, Followed by an Open-Label Period and a Subsequent Long-Term Administration Study.. Life (Basel, Switzerland). https://doi.org/10.3390/life15081168

Source records

pubmed · retrieved 2026-09-26T11:28:20.511Z