Risdiplam therapy in adult patients with Spinal muscular Atrophy (SMA). A 24-month-real-world experience at a single muscular centre.

Cesarone E, Picillo E, Scutifero M, Passamano L, Nigro V

DOI: 10.36185/2532-1900-2280
Published: 2026 Mar
Container: Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.36185/2532-1900-2280,
  title = {Risdiplam therapy in adult patients with Spinal muscular Atrophy (SMA). A 24-month-real-world experience at a single muscular centre.},
  author = {Cesarone E and Picillo E and Scutifero M and Passamano L and Nigro V},
  year = {2026},
  journal = {Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology},
  doi = {10.36185/2532-1900-2280},
  url = {https://doi.org/10.36185/2532-1900-2280}
}

RIS

TY  - JOUR
TI  - Risdiplam therapy in adult patients with Spinal muscular Atrophy (SMA). A 24-month-real-world experience at a single muscular centre.
AU  - Cesarone E
AU  - Picillo E
AU  - Scutifero M
AU  - Passamano L
AU  - Nigro V
PY  - 2026
JO  - Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology
DO  - 10.36185/2532-1900-2280
UR  - https://doi.org/10.36185/2532-1900-2280
ER  -

APA

E, C., E, P., M, S., L, P., & V, N. (2026). Risdiplam therapy in adult patients with Spinal muscular Atrophy (SMA). A 24-month-real-world experience at a single muscular centre.. Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology. https://doi.org/10.36185/2532-1900-2280

Source records

pubmed · retrieved 2026-09-26T17:07:15.973Z