CD117 epitope-shielded hematopoietic stem cell transplantation with toxin-free conditioning and in vivo selection ameliorates a β-thalassemia model.

Marone R, Lepore R, Paschoudi K, Zuin J, Sinopoli A, Camus A, Burgold T, Bartoszek E, Calabrese D, Toranelli M, Wittwer J, Rhiel M, Andrieux G, Li C, Hsu A, Wiederkehr A, Wellinger LC, Grossjohann EM, Buren ET, Brault J, Prat LG, Lehmann F, Sacramento VD, Divsalar C, Yumlu S, Liu DR, Lieber A, Cathomen T, Cornu TI, Yannaki E, Urlinger S, Jeker LT

Open source

DOI: 10.64898/2026.07.07.736903
Published: 2026 Jul 8
Container: bioRxiv : the preprint server for biology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.64898/2026.07.07.736903,
  title = {CD117 epitope-shielded hematopoietic stem cell transplantation with toxin-free conditioning and in vivo selection ameliorates a β-thalassemia model.},
  author = {Marone R and Lepore R and Paschoudi K and Zuin J and Sinopoli A and Camus A and Burgold T and Bartoszek E and Calabrese D and Toranelli M and Wittwer J and Rhiel M and Andrieux G and Li C and Hsu A and Wiederkehr A and Wellinger LC and Grossjohann EM and Buren ET and Brault J and Prat LG and Lehmann F and Sacramento VD and Divsalar C and Yumlu S and Liu DR and Lieber A and Cathomen T and Cornu TI and Yannaki E and Urlinger S and Jeker LT},
  year = {2026},
  journal = {bioRxiv : the preprint server for biology},
  doi = {10.64898/2026.07.07.736903},
  url = {https://doi.org/10.64898/2026.07.07.736903}
}

RIS

TY  - JOUR
TI  - CD117 epitope-shielded hematopoietic stem cell transplantation with toxin-free conditioning and in vivo selection ameliorates a β-thalassemia model.
AU  - Marone R
AU  - Lepore R
AU  - Paschoudi K
AU  - Zuin J
AU  - Sinopoli A
AU  - Camus A
AU  - Burgold T
AU  - Bartoszek E
AU  - Calabrese D
AU  - Toranelli M
AU  - Wittwer J
AU  - Rhiel M
AU  - Andrieux G
AU  - Li C
AU  - Hsu A
AU  - Wiederkehr A
AU  - Wellinger LC
AU  - Grossjohann EM
AU  - Buren ET
AU  - Brault J
AU  - Prat LG
AU  - Lehmann F
AU  - Sacramento VD
AU  - Divsalar C
AU  - Yumlu S
AU  - Liu DR
AU  - Lieber A
AU  - Cathomen T
AU  - Cornu TI
AU  - Yannaki E
AU  - Urlinger S
AU  - Jeker LT
PY  - 2026
JO  - bioRxiv : the preprint server for biology
DO  - 10.64898/2026.07.07.736903
UR  - https://doi.org/10.64898/2026.07.07.736903
ER  -

APA

R, M., R, L., K, P., J, Z., A, S., A, C., T, B., E, B., D, C., M, T., J, W., M, R., G, A., C, L., A, H., A, W., LC, W., EM, G., ET, B., J, B., LG, P., F, L., VD, S., C, D., S, Y., DR, L., A, L., T, C., TI, C., E, Y., S, U., & LT, J. (2026). CD117 epitope-shielded hematopoietic stem cell transplantation with toxin-free conditioning and in vivo selection ameliorates a β-thalassemia model.. bioRxiv : the preprint server for biology. https://doi.org/10.64898/2026.07.07.736903

Source records

pubmed · retrieved 2026-09-25T06:11:19.202Z