RNA trans-splicing treatment for Duchenne muscular dystrophy

Ryan H. Hsu, Claire E. Williams, Geraldine Maier, Miriam Gullo, Karen Lettieri, Cindy J. Alvarez, Kip J. Hermann, Stella Kramer, Satchidananda Panda, Lukas C. Bachmann, Samuel L. Pfaff

Open source

DOI
10.64898/2026.09.13.751281
Published
2026-09-16
Container
Not recorded
Publisher
openRxiv
Open access
unknown

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BibTeX

@article{allodium:10.64898/2026.09.13.751281,
  title = {RNA trans-splicing treatment for Duchenne muscular dystrophy},
  author = {Ryan H. Hsu and Claire E. Williams and Geraldine Maier and Miriam Gullo and Karen Lettieri and Cindy J. Alvarez and Kip J. Hermann and Stella Kramer and Satchidananda Panda and Lukas C. Bachmann and Samuel L. Pfaff},
  year = {2026},
  doi = {10.64898/2026.09.13.751281},
  url = {https://doi.org/10.64898/2026.09.13.751281}
}

RIS

TY  - JOUR
TI  - RNA trans-splicing treatment for Duchenne muscular dystrophy
AU  - Ryan H. Hsu
AU  - Claire E. Williams
AU  - Geraldine Maier
AU  - Miriam Gullo
AU  - Karen Lettieri
AU  - Cindy J. Alvarez
AU  - Kip J. Hermann
AU  - Stella Kramer
AU  - Satchidananda Panda
AU  - Lukas C. Bachmann
AU  - Samuel L. Pfaff
PY  - 2026
DO  - 10.64898/2026.09.13.751281
UR  - https://doi.org/10.64898/2026.09.13.751281
ER  - 

APA

Hsu, R. H., Williams, C. E., Maier, G., Gullo, M., Lettieri, K., Alvarez, C. J., Hermann, K. J., Kramer, S., Panda, S., Bachmann, L. C., & Pfaff, S. L. (2026). RNA trans-splicing treatment for Duchenne muscular dystrophy. https://doi.org/10.64898/2026.09.13.751281

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