In vivo HSPC gene therapy of hemoglobinopathies without drug selection of corrected cells.

Sakunthala Velmurugan A, Paschoudi K, Queenan JA, Gil S, Maynard A, Fontana CE, Sharma R, Long A, Li C, Wang H, Anderson AK, Georgakopoulou A, Psatha N, Giannaki M, Vlachaki E, Ahmed N, Sousa AA, Liu DR, Yannaki E, Lieber A, Karuppusamy KV

Open source

DOI: 10.64898/2026.09.15.751289
Published: 2026 Sep 17
Container: bioRxiv : the preprint server for biology
Publisher: Not recorded
Open access: yes

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Cite this work

BibTeX

@article{allodium:10.64898/2026.09.15.751289,
  title = {In vivo HSPC gene therapy of hemoglobinopathies without drug selection of corrected cells.},
  author = {Sakunthala Velmurugan A and Paschoudi K and Queenan JA and Gil S and Maynard A and Fontana CE and Sharma R and Long A and Li C and Wang H and Anderson AK and Georgakopoulou A and Psatha N and Giannaki M and Vlachaki E and Ahmed N and Sousa AA and Liu DR and Yannaki E and Lieber A and Karuppusamy KV},
  year = {2026},
  journal = {bioRxiv : the preprint server for biology},
  doi = {10.64898/2026.09.15.751289},
  url = {https://doi.org/10.64898/2026.09.15.751289}
}

RIS

TY  - JOUR
TI  - In vivo HSPC gene therapy of hemoglobinopathies without drug selection of corrected cells.
AU  - Sakunthala Velmurugan A
AU  - Paschoudi K
AU  - Queenan JA
AU  - Gil S
AU  - Maynard A
AU  - Fontana CE
AU  - Sharma R
AU  - Long A
AU  - Li C
AU  - Wang H
AU  - Anderson AK
AU  - Georgakopoulou A
AU  - Psatha N
AU  - Giannaki M
AU  - Vlachaki E
AU  - Ahmed N
AU  - Sousa AA
AU  - Liu DR
AU  - Yannaki E
AU  - Lieber A
AU  - Karuppusamy KV
PY  - 2026
JO  - bioRxiv : the preprint server for biology
DO  - 10.64898/2026.09.15.751289
UR  - https://doi.org/10.64898/2026.09.15.751289
ER  -

APA

A, S. V., K, P., JA, Q., S, G., A, M., CE, F., R, S., A, L., C, L., H, W., AK, A., A, G., N, P., M, G., E, V., N, A., AA, S., DR, L., E, Y., A, L., & KV, K. (2026). In vivo HSPC gene therapy of hemoglobinopathies without drug selection of corrected cells.. bioRxiv : the preprint server for biology. https://doi.org/10.64898/2026.09.15.751289

Source records

pubmed · retrieved 2026-09-25T08:14:18.882Z
europe-pmc · retrieved 2026-09-25T08:14:18.890Z